Gaucher Disease Treatment
Can this condition be treated? What Gaucher Disease treatment options are available? Learn more below about the current treatments available to patients.
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How to Treat Gaucher Disease
There is no treatment for the severe neurologic symptoms that may occur with type II and type III Gaucher. However, new treatment options for type I Gaucher include:
- Enzyme replacement therapy-This consists of a regular infusion with an enyzme replacement medicine. Examples of these medicines include alglucerase (derived from human cells), velaglucerase alfa (derived from human cells), and imiglucerase (chemically-modified enzyme). This therapy can help reduce skeletal abnormalities, liver and spleen size, and reverse some abnormal blood counts.
- Substrate reduction therapy-Miglustat (Zavesca) has been approved by the US Food and Drug Administration for treatment of type I Gaucher disease in adults who cannot receive hormone replacement therapy.
- Bone marrow transplant-A transplant is used only in patients with severe clinical symptoms and bone abnormalities. If it is successful, it provides a lifelong cure.
- Splenectomy -The surgical removal of the spleen may be done if enzyme replacement therapy is not available.
© 2009 Nucleus Medical Media, Inc.
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implied to be a substitute for professional medical advice. CALL YOUR HEALTHCARE PROVIDER IMMEDIATELY IF YOU THINK YOU MAY HAVE A
MEDICAL EMERGENCY. Always seek the advice of your physician or other qualified health provider prior to starting any new treatment
or with any questions you may have regarding a medical condition. Copyright ©2013 EBSCO Publishing All rights
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